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Turning the tide for rare disease

Rare disease champions: how Cycle Pharmaceuticals and their partner Inceptua are redefining pharmaceutical philanthropy and opening up access to novel therapies in low and middle-income regions

By Becky Pender
15 January 2025

RARE caregiving

Challenges of caring for a rare disease patient—a discussion

By Becky Pender
20 November 2024

Charity & advocacy

NF1 breast cancer awareness campaign: Leading NF1 expert Professor Gareth Evans calls for earlier screening

By Becky Pender
15 October 2024

Charity & advocacy

NF1 breast cancer awareness campaign: Caitriona Plunkett empowers young women with NF1 to prioritise breast health

By Becky Pender
15 October 2024

RARE News

International Gaucher Alliance celebrates 30 years of international patient advocacy

By Becky Pender
23 September 2024
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