Close
×
Subscribe Now
By entering these details you are signing up to receive our newsletter.
First Name
Last Name
Your Email
Type of visitor?
Individuals with a rare condition
Caregiver/family member
Industry/biotech/pharma
Healthcare professionals
Charity/advocate
General interest
Newsletters
RAREBite Newsletter Subscribers (Twice Weekly)
Magazine and RARE Round-Up Weekly Newsletter
Latest Edition
RARE and Under-Funded
Subscribe Now
Home
Meet the team
Magazine
RARE INSIGHTS
A day in the life
Charity & advocacy
Industry insights
Letters
Medical
News
Patient voice
RARE caregiving
RARE ramblings
RARE REV-inar
Reviews
Science & tech
Sunday sessions
Turning the tide for rare disease
THE PEOPLE OF RARE
Digital Spotlight
RARE Reports
Resources
Charity Partners
WORK WITH US
Rare Revolutionaries
Community Gallery
Rare Youth
SHOP
Latest Edition
RARE and Under-Funded
Subscribe Now
To use more accessibility options, please use a different browser such as Chrome or Firefox.
Letters
Letters
A troubling development in access to treatment for people living with primary biliary cholangitis (PBC)
By CONTRIBUTOR
7 August 2024
RARE News
Timothy Syndrome Alliance (TSA) looks to recruit Trustee
By admin
2 August 2024
RARE News
CMT Research Foundation invests in project at nationwide children’s hospital to develop improved gene therapy delivery systems for several types of CMT
By admin
1 August 2024
Industry Insights
Cell and gene therapies: Where are we now?
By CONTRIBUTOR
31 July 2024
RARE News
Our Voice, Our Rights, Our Future: The ALLIANCE report and video explores key themes and feedback from its 2024 annual conference
By admin
31 July 2024
RARE News
Innov4-ePiK: Innovative diagnostic and therapeutic approaches in potassium channel developmental and epileptic encephalopathies (K-DEEs) using 4P for medicine
By admin
29 July 2024
RARE News
cTAP Study indicates Duchenne muscular dystrophy clinical trial enrollment criteria should expand beyond ambulatory status
By admin
29 July 2024
RARE News
Landmarks shine pink and purple for National Eosinophilic Week
By admin
29 July 2024
Letters
Sarcoma Awareness Month: Sarcomas demand urgent awareness and education to prevent poor outcomes
By CONTRIBUTOR
24 July 2024
Turning the tide for rare disease
I am Celine Dion: The stiff person syndrome community reacts to the release of Dion’s documentary
By CONTRIBUTOR
22 July 2024
RARE News
The CMT Research Foundation’s 2024 Global CMT Research Convention to gather renowned scientific experts and patients to discuss status of treatments and cures for Charcot-Marie-Tooth (CMT) disease
By admin
19 July 2024
RARE News
NHL All-Star Ryan Getzlaf returns to the links for the 13th Annual Getzlaf Golf Shootout on September 13-14, benefiting CureDuchenne
By admin
17 July 2024
Industry Insights
Early access to medicines: A picture is worth a thousand words
By CONTRIBUTOR
17 July 2024
RARE News
Challenges and priorities for the PSP and CBD community: Insights from Mark Jackson
By admin
12 July 2024
RARE News
The CMT Research Foundation to launch grant program to support young investigators working on CMT
By admin
12 July 2024
Charity & advocacy
Bridging gaps in care: How independent charitable patient assistance organisations support underserved populations
By CONTRIBUTOR
10 July 2024
RARE News
Concerned stakeholders issue call to action on the implementation of the EU Joint Clinical Assessment for ATMPs
By admin
9 July 2024
« Previous
1
2
3
4
…
30
Next »
Skip to content
Open toolbar
Accessibility Tools
Accessibility Tools
Increase Text
Increase Text
Decrease Text
Decrease Text
Grayscale
Grayscale
High Contrast
High Contrast
Negative Contrast
Negative Contrast
Light Background
Light Background
Links Underline
Links Underline
Readable Font
Readable Font
Reset
Reset